As we kick off 2025, we wanted to take a moment to reflect on the past year. We all feel a deep sense of gratitude to the Duchenne muscular dystrophy (DMD) community. You have been open and honest as we strive to understand your needs and desires. We are awed by the dedication, the smarts, and the fortitude of so many people we have encountered. Devoted siblings, selfless moms and dads, exuberant boys, determined young men, loving grandparents, innovative advocacy leaders, knowledgeable physicians, compassionate physical therapists – so many of you have meaningfully informed our ongoing effort to determine how we can best serve this community.

One thing we know is this: There’s no single solution to change the face of Duchenne. We all have to continue working really hard – together – to keep making strides against this disease. We need teamwork, we need trust, and we need honest discussions to keep moving forward to conquer Duchenne. In 2024, you really came through by welcoming us to the community and guiding us to be the best we can be. We look forward to continuing our collaboration with all of you this year so we can strengthen and improve what we are already doing and expand our reach to help even more families.

We introduced our team blog in July 2024, just a few days after our treatment for DMD became available to eligible patients. Our intent with the blog is to connect with the community we serve on a personal level. We want the people who are directly affected by our actions to know who we are, what we care about, and what we are working on. Sometimes we share personal reflections, like Scott’s September post called “What Makes an Expert?” and Matt’s entry in November about being a guest in the Duchenne community. Other times we highlight important information we hope you will find useful, like Stephanie’s post about access resources and the Top Ten list Caroline shared just a few days after our DMD treatment was made commercially available. We also want you to know how we approach the work we do, which is why Dan wrote about weaving the patient experience into our marketing efforts and Melinda shared her thoughts on the exciting challenge of building a mission-focused company.

As we head into the new year, we want to know if we are hitting the mark in terms of what you want to hear from us. So if you have space for one more New Year’s resolution on your list, please add “get in touch with ITF.” Do you have a question about our work? Is there something you want to know more about? Do you have a story you feel we should hear about how Duchenne affects your life? Drop us a line, because the more we know, the better we can do.

From all of us at ITF, we wish you a very happy New Year, and we look forward to connecting in 2025!

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