FDA Approval Granted, Access Denied – Now What?
By Stephanie Trafton
Head of US Value & Access
10/4/24
The United States of America is famous for medical innovation. Our country leads the world in the number of new drugs and medical devices that are given the green light by our government. Unfortunately, this does not mean that every approved new... Read More
What Makes an Expert?
By Scott Baver
Vice President, Head of US Medical Affairs
9/23/24
I have been studying neuroscience and working in the field of neuromuscular disease for more than 20 years. I may have the academic degrees and the work experience to qualify as an "expert," but there's no doubt in my mind that the real experts are you... Read More
A Good Day
By Caroline Allen
Head, US Patient Advocacy & Communications
7/25/24
In the long path to new treatments for Duchenne, today is a good day. A new medicine that is designed to interfere with Duchenne’s relentless progression is now officially available in the United States. While I am feeling positive and hopeful because of this... Read More